Research Journal of Pharmacy and Technology
SCOPUS
  • Year: 2024
  • Volume: 17
  • Issue: 5

A review of the state of drug development for uncommon diseases and its future potential

1Associate Professor, Department of EEE, Holy Mary Institute of Technology and Science, Hyderabad, Telangana, India

2Professor and Director, Department of Electronics and Communication Engineering, Holy Mary Institute of Technology and Science, Hyderabad, Telangana, India

*Corresponding Author E-mail: sathishk0711@gmail.com

Online published on 13 June, 2024.

Abstract

This article discusses the development of drugs for uncommon diseases as well as the future prospects for these drugs. When developing treatments for uncommon diseases, there are several challenges that must be overcome. Among them are limited patient populations, a lack of understanding of uncommon diseases, and regulatory hurdles. Regulatory incentives and advancements in drug development are discussed in addition to the use of biomarkers and repurposing existing drugs. Patients suffering from uncommon diseases need innovation and collaboration.

Keywords

Uncommon diseases, Development of drugs, Molecular biology, Therapies involving gene editing, Orphan drugs